SURE

Holida, Myrl, Linhart, Aleš, Longo, Nicola, Wallace, Eric, Tøndel, Camilla, Hughes, Derralynn, Warnock, David G., Pisani, Antonio, Eyskens, François, Deegan, Patrick, Feldt-Rasmussen, Ulla, Goker-Alpan, Ozlem, Mehta, Ankit, Piotti, Giovanni, Fichera, Vito, Wang, Meng, Chertkoff, Raul, Waldek, Stephen, Wilcox, William R. and Bernat, John A. (2026) Long-term efficacy and safety of pegunigalsidase alfa administered every 4 weeks in adults with Fabry disease: results from up to 5 years of the BRIGHT F51 phase III, open-label extension study. Orphanet Journal of Rare Diseases, 21 (1): 185. p. 185. ISSN 1750-1172